Translational Research in Muscular Dystrophy
This book presents recent advances in translational research on muscular dystrophy (MD) to physicians and researchers, including cutting-edge research on the disease such as regenerative medicine, next-generation DNA sequencing, and nucleic acid therapies. It also describes the current systems for c...
Clasificación: | Libro Electrónico |
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Autor Corporativo: | |
Otros Autores: | , , |
Formato: | Electrónico eBook |
Idioma: | Inglés |
Publicado: |
Tokyo :
Springer Japan : Imprint: Springer,
2016.
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Edición: | 1st ed. 2016. |
Temas: | |
Acceso en línea: | Texto Completo |
Tabla de Contenidos:
- 1. Fukuyama congenital muscular dystrophy - Clinical aspects
- 2. α-Dystroglycanopathy
- 3. Myotonic dystrophy
- 4. Molecular pathogenesis and therapeutic strategy in GNE myopathy
- 5. Targeting the type I TGF-β receptor for treating caveolin-3-deficient autosomal dominant limb-girdle muscular dystrophy type 1C and muscle wasting disorders
- 6. Translational Research in Nucleic Acid Therapies for Muscular Dystrophies
- 7. Toward regenerative medicine for muscular dystrophies-Lessons from regeneration processes-
- 8. Stem cell-based therapy for Duchenne muscular dystrophy
- 9. Therapeutic approach of iPS cell technology for treating muscular dystrophy
- 10. Clinical aspects of GNE myopathy and translational medicine
- 11. Patient registries for international harmonized clinical development
- 12. Muscular Dystrophy Clinical Trial Network in Japan
- 13. Translational research on DMD in Japan From mice to exploratory investigator-initiated clinical trial in humans. .