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Rare diseases : challenges and opportunities for social entrepreneurs /
There are 7,000 rare diseases affecting 6% - 8% of the global population. That's 3.5 million people in the UK alone. Yet only 200 rare diseases have approved treatments. In recent years, there has been a surge of interest from business and social entrepreneurs in the field of health - including...
| Clasificación: | Libro Electrónico |
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| Otros Autores: | |
| Formato: | Electrónico eBook |
| Idioma: | Inglés |
| Publicado: |
Sheffield, England :
Greenleaf Publishing,
2013.
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| Temas: | |
| Acceso en línea: | Texto completo |
Tabla de Contenidos:
- Cover; Half title; Title; Copyright; Contents; Introduction; 1Toward a focused, multinational, rare disease awareness initiative; 2The challenges of scaling up an orphan drug enterprise; 3Building an entrepreneurial patient movement; 4The practicalities of clinical development of drugs for rare diseases; 5Navigating orphan drugs through the regulatory maze; 6Drug repositioning strategies for rare and orphan diseases; 7Why patient registries are crucial for finding cures for rare diseases.
- 8 Challenges, strategies and lessons learned for the setting up and running of a European Reference Network for rare disease9Managing research advances into a rare disease; 10The BLACKSWAN Foundation for rare diseases; 11The rise and fall of Sanfilippo syndrome; 12Lobbying for a national rare disease plan in the UK; 13The global drug development process; Conclusion; Index; Back cover.